Hurler Syndrome Pathway
March 17, 2025
Mucopolysaccharidosis Type I - Symptoms, Causes, Treatment | NORD Bone, joint and tooth development in mucopolysaccharidoses: Relevance to therapeutic options - ScienceDirect A Highly Efficacious PS Gene Editing System Corrects Metabolic and Neurological Complications of Mucopolysaccharidosis Type I: Molecular Therapy Hurler Syndrome Pathway